TY  - BOOK
AU  - Engelhardt, John||Ferec, Claude||Yan, Ziying
TI  - Molecular Basis and Gene Therapies of Cystic Fibrosis
KW  - cystic fibrosis||Staphylococcus aureus||superantigen||enterotoxin gene cluster||MRSA||exosomes||microvesicles||lung||primary cells||newborn screening||trypsinogen||CFTR gene||next generation sequencing||health policy||rAAV2/HBoV1||baculovirus||insect cells||lung microbiome||metagenomics||gut–lung axis||Cystic fibrosis||CFTR||transcriptomics||proteostasis||small molecules||drug development||common and new pathogenic variants||ethnic Russian population||gene therapy||cyclophosphamide||transient immunosuppression||incidence||survival||genotype-phenotype correlations||health policies||CFTR modulators||human nasal epithelial cells||organoids||biomarker||functional assay||pre-clinical in vitro models||CFTR-related disorders||molecular diagnosis||CFTR variants||Next Generation Sequencing (NGS)||disease liability||interpretation||penetrance||genotype-guided therapy||miRNA||airway basal cell||lentivirus
UR  - https://mdpi.com/books/pdfview/book/3205
ER  -